Expanding therapeutic options for Pompe disease: a new small molecule inhibitor of glycogen synthase 1 (GYS1) shows preclinical promise in Pompe disease
@article{ATM131058,
author = {Rebecca L. Koch and Benjamin T. Cocanougher and Jeong-A Lim and Nina Raben and Priya S. Kishnani},
title = {Expanding therapeutic options for Pompe disease: a new small molecule inhibitor of glycogen synthase 1 (GYS1) shows preclinical promise in Pompe disease},
journal = {Annals of Translational Medicine},
volume = {12},
number = {6},
year = {2024},
keywords = {},
abstract = {},
issn = {2305-5847}, url = {https://atm.amegroups.org/article/view/131058}
}