Expanding therapeutic options for Pompe disease: a new small molecule inhibitor of glycogen synthase 1 (GYS1) shows preclinical promise in Pompe disease
@article{ATM131058, author = {Rebecca L. Koch and Benjamin T. Cocanougher and Jeong-A Lim and Nina Raben and Priya S. Kishnani}, title = {Expanding therapeutic options for Pompe disease: a new small molecule inhibitor of glycogen synthase 1 (GYS1) shows preclinical promise in Pompe disease}, journal = {Annals of Translational Medicine}, volume = {12}, number = {6}, year = {2024}, keywords = {}, abstract = {}, issn = {2305-5847}, url = {https://atm.amegroups.org/article/view/131058} }